A breakthrough gene therapy treatment for Haemophilia A has been shown to offer long-term benefits that have already transformed the lives of 13 men in the UK. Clinical researchers led by Professor John Pasi from Queen Mary University of London first announced in 2017 that 85% of men treated with a single infusion of a […]
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‘Trailblazing’ haemophilia drug will be available on NHS England
NHS agrees to pay for a ‘trailblazing’ drug that prevents deadly bleeds in patients with severe haemophilia Severe haemophilia A is thought to affect around 1,800 people in the UK Patients were forced to have clotting drugs administered into vein in chest Drug emicizumab can be injected under the skin as little as every two weeks […]